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Neuren Phase 2 trial shows significant improvements in Pitt Hopkins syndrome

  • Written by PR Newswire

Highlights:

  • Statistically significant improvement from baseline assessed by both clinicians and caregivers in all four efficacy measures specifically designed for Pitt Hopkins syndrome (Wilcoxon signed rank test p<0.05)
  • Clinician and caregiver global efficacy measures showed a level of improvement considered clinically meaningful:

- Clinical...

Read more: Neuren Phase 2 trial shows significant improvements in Pitt Hopkins syndrome

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